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Leaders in Genetic

Many employees in the lab wearing white lab coats and smiling at the camera

Leaders in Genetic

We are advancing our proprietary genetic medicines platform as we seek to transform the lives of patients with rare diseases by addressing the underlying cause of the disease.

Our Company is based on an important scientific discovery – a family of 15 adeno-associated virus vectors derived from human hematopoietic stem cells (AAVHSCs) that are designed to precisely and efficiently deliver genetic medicines in vivo either through gene therapy or nuclease-free gene editing, as well as to deliver one-time gene therapy to produce antibodies throughout the body through the GTx-mAb platform.

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The Team

Homology Medicines has a team of experienced and dedicated leaders in rare diseases and genetic medicines to translate our technology into treatments for patients.

Board of

Scientific Advisory