Biodistribution and Tolerability of HMI102, a Novel AAVHSC15 Encoding Human Phenylalanine Hydroxylase, in Cynomolgus Monkeys

Biodistribution and Tolerability of HMI102, a Novel AAVHSC15 Encoding Human Phenylalanine Hydroxylase, in Cynomolgus Monkeys

Wright TL, Ellsworth JL, Ahmed SS, et al.