Blood-Brain-Barrier Crossing Leads to Long-Term Efficacy in the CNS of HMI-203: Gene Therapy Development Candidate for Mucopolysaccharidosis Type II (MPS II), or Hunter Syndrome
Smith L, Patel K, Gingras J, et al. ESGCT 2021.
Smith L, Patel K, Gingras J, et al. ESGCT 2021.