Genome-Wide Integration Assay for rAAV Mediated Homologous Recombination (HR) in Human Hepatocytes Demonstrated Precision of In Vivo Gene Editing Approach

Genome-Wide Integration Assay for rAAV Mediated Homologous Recombination (HR) in Human Hepatocytes Demonstrated Precision of In Vivo Gene Editing Approach

Thompson J, Von Stetina J, Prout J, et al. ASHG 2021.