Impact of Full and Empty Particle Concentration on Product Quality and in vivo Efficacy of HMI-102 in a Mouse Model of Phenylketonuria (PKU)
Faulkner E, Adamson-Small L, Ahmed S, et al. ESGCT 2019.
Faulkner E, Adamson-Small L, Ahmed S, et al. ESGCT 2019.