Long-Term Systemic Expression and Cross-Correction Ability of HMI-203, Investigational Gene Therapy Candidate for Mucopolysaccharidosis Type II (MPS II), or Hunter Syndrome
Patel K, Smith L, Gingras J, Tzianabos A, et al. ASHG 2021.
Patel K, Smith L, Gingras J, Tzianabos A, et al. ASHG 2021.