Nuclease-Free Genome Editing by AAVHSC Vectors Leads to In Vivo Genome Correction and Amelioration of Disease Phenotype in a Mouse Model of Phenylketonuria (PKU)
Nuclease-Free Genome Editing by AAVHSC Vectors Leads to In Vivo Genome Correction and Amelioration of Disease Phenotype in a Mouse Model of Phenylketonuria (PKU)