Patient-Focused Drug Development for a Single Intravenous Dose of HMI-203 Gene Therapy in Adult Mucopolysaccharidosis (MPS) II, or Hunter Syndrome, Patients
Haroldson J, Witalisz CJ, Martin R,. et al. ASHG 2021.
Haroldson J, Witalisz CJ, Martin R,. et al. ASHG 2021.