Patients & Families

Homology Medicines is focused on advancing our genetic medicines platform as one-time treatments and potential cures for patients with rare diseases

Patients & Families

We are advancing our proprietary genetic medicines platform as we seek to transform the lives of patients with rare diseases by targeting or addressing the underlying cause of the disease. The person, family members and caregivers affected by rare disease are the biggest drivers in every decision our Company makes. From hiring new employees to determining new research initiatives to beginning development programs, we consider the patient community first and foremost.

We continuously seek opportunities to learn from the patients we serve and to provide opportunities to share information about our programs. While we are still in the early stages of clinical development, we are moving forward as quickly as possible, knowing that there are people waiting on new advances. You can learn more about our therapeutic areas or email your questions to

Patient Advocacy Contact


Cara Mayfield

Vice President, Patient Advocacy &
Corporate Communications

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Patient & Family Resources

Phenylketonuria (PKU)

national pku alliance logo
necpad logo
mid-atlantic connection logo
PKU org of IL logo
TN pku foundation logo
pku northwest logo
CA coalition logo
Canadian pku logo
GA connect logo
gap logo
intermountain pku logo

MPS II (Hunter syndrome)

project alive logo
national mps logo
canadian mps logo
mps argentina logo

Metachromatic Leukodystrophy (MLD)

calliope joy logo
mld foundation logo
cure mld logo
united leukodystrophy foundation logo
global leukdytrophy initiative logo

Paroxysmal Nocturnal Hemoglobinuria (PNH)

aa mds logo

Rare Disease

everyday life foundation logo
rare new england logo
dash alliance logo

Community Involvement

The Homology team participates in events to raise awareness of rare disease and support patient advocacy organizations.

Click to see why Homology wears blue for PKU!