Patients & Families

Homology Medicines is focused on advancing our genetic medicines platform as one-time treatments and potential cures for patients with rare diseases

Patients & Families

We are advancing our proprietary genetic medicines platform as we seek to transform the lives of patients with rare diseases by targeting or addressing the underlying cause of the disease. The person, family members and caregivers affected by rare disease are the biggest drivers in every decision our Company makes. From hiring new employees to determining new research initiatives to beginning development programs, we consider the patient community first and foremost.

We continuously seek opportunities to learn from the patients we serve and to provide opportunities to share information about our programs. While we are still in the early stages of clinical development, we are moving forward as quickly as possible, knowing that there are people waiting on new advances. You can learn more about our therapeutic areas or email your questions to patientadvocacy@homologymedicines.com.

Patient Advocacy Contact

Cara Mayfield

Vice President, Patient Advocacy &
Corporate Communications

Patient & Family Resources

Phenylketonuria (PKU)

MPS II (Hunter syndrome)

Metachromatic Leukodystrophy (MLD)

Paroxysmal Nocturnal Hemoglobinuria (PNH)

Rare Disease

Community Involvement

The Homology team participates in events to raise awareness of rare disease and support patient advocacy organizations.

Click to see why Homology wears blue for PKU!

Homology team at NECPAD’s annual “Fast Feet for Phreedom 5K” to kick off PKU awareness month!

In recognition of Rare Disease Day, our team learned about the day-to-day burden of living with a rare disease. We came together in our Zebra stripes to honor the community and show our support

We had the honor of listening to guest speaker, Kyle E. Underwood, MHA, who shared his inspiring story during our Rare Disease Day event

In recognition of Rare Disease Day, we partnered with TinySuperheroes to sponsor and deliver personalized superhero capes to children overcoming an illness or disability. We wrote motivational letters and created artwork for each child to honor their bravery

Homology team members volunteering at Cradles to Crayons

Some of the many Homology participants who ran NECPAD’s 2020 Virtual Victory 5K during PKU Awareness Month to raise funds for research and raise awareness of PKU

Homology employees tackled the PKU diet in solidarity with the PKU Community to honor Rare Disease Day

Homology team with guest speaker Maria Kefalas, who shared her experiences as a mother of a child with MLD and the work her organization, the Calliope Joy Foundation, does to support MLD families

Homology employees recognizing Rare Disease Day, wearing color-coded shirts to demonstrate who has been personally impacted by rare disease themselves or by their immediate family / friends

Awesome participation from the Homology team at NECPAD’s 2019 Fast Feet for Phreedom 5K

Homology runners after completing the Fast Feet for Phreedom 5K

The Homology team wearing purple to recognize MLD awareness month