Single Intravenous Dose of AAVHSC15 Packaging a Human Phenylalanine Hydroxylase Transgene Results in Durable Correction of Phenylketonuria In Vivo
Francone OL, Ahmed SS, Ellsworth JL, et al. WORLDSymposium 2019.
Francone OL, Ahmed SS, Ellsworth JL, et al. WORLDSymposium 2019.