Sustained Correction of a Murine Model of Phenylketonuria and Integration Into the Genome Following a Single Administration of an AAVHSC15 Phenylalanine Hydroxylase Gene Editing Vector

Sustained Correction of a Murine Model of Phenylketonuria and Integration Into the Genome Following a Single Administration of an AAVHSC15 Phenylalanine Hydroxylase Gene Editing Vector

Benard L, Lamppu D, Von Stetina JR, et al.