Sustained Correction of a Murine Model of Phenylketonuria and Integration Into the Genome Following a Single Administration of an AAVHSC15 Phenylalanine Hydroxylase Gene Editing Vector
Benard L, Lamppu D, Von Stetina JR, et al. ASGCT 2022.
Benard L, Lamppu D, Von Stetina JR, et al. ASGCT 2022.